THE MOST IMPORTANT ORPHAN DRUG EVENT WORLDWIDE

27 October 2025 | Workshop Day
28-29 October 2025 | Conference & Exhibition

RAI Congress Centre, Amsterdam

Strategy, Advocacy & Partnering For The Global Orphan Drug Industry

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The World Orphan Drug Congress is the largest and most established orphan drug & rare disease meeting of its kind across the globe.

From cell and gene therapy, genetic testing, and market access, to real world evidence, this one meeting covers the whole orphan drugs value chain where science, government and manufacturers all come together to create groundbreaking progress.

We will continue to cover orphan drug progress in:

Cell & Gene Therapy

Gene Testing

Market Access

Epidemiology & Forecasting

Real World Evidence

Global Patient Advocacy

Orphan Drugs Policy

and more